Supports studies that develop mature ideas and expand key discoveries in bone marrow failure research and patient care. Funds translational and clinical research including preclinical models, human data, and correlative studies linked to clinical trials, excluding clinical trials themselves. Supports IND-enabling efforts such as lead compound characterization and toxicology. Allows partnering PIs with distinct application requirements and mandates preliminary data.
Open to any type of entity without restrictions, subject to additional clarifications. No specific eligibility limitations stated.